In a global first, gene therapy that could prove life-saving for children has been recommended for approval in Europe.
The pioneering technology to fix faulty genes has been developed by Italian scientists and GlaxoSmithKline
FOX News reports:
The European Medicines Agency (EMA) said on Friday it had endorsed the therapy, called Strimvelis, for a tiny number of children with ADA Severe Combined Immune Deficiency (ADA-SCID) for whom no matching bone marrow donor is available.
Around 15 children a year are born in Europe with the ultra-rare genetic disorder, which leaves them unable to make a type of white blood cell. They rarely survive beyond two years unless their immune function is restored with a suitable bone marrow transplant.